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Spark Therapeutics
Spark Therapeutics
(ONCE)
Spark Therapeutics, Inc. is a developer of gene therapy treatments, which treat debilitating genetic diseases. It is a subsidiary of Hoffmann-La Roche.
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
All
Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Luxturna
Voretigene neparvovec
2017-12-19
Retinitis pigmentosa
,
Leber congenital amaurosis
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Voretigene neparvovec
retinal dystrophies
Bevifimod
recurrence
,
acute disease
,
philadelphia chromosome
,
neoplasm metastasis
,
squamous cell neoplasms
,
neoplasms
,
myeloid leukemia acute
,
myeloid leukemia
,
lymphoma
,
carcinoma
,
breast neoplasms
,
mantle-cell lymphoma
,
precursor cell lymphoblastic leukemia-lymphoma
,
myelodysplastic syndromes
,
syndrome
,
hepatocellular carcinoma
,
liver neoplasms
,
prostatic neoplasms
,
pancreatic neoplasms
,
glioblastoma
,
melanoma
,
neuroendocrine carcinoma
,
papillary thyroid cancer
,
primary myelofibrosis
,
ankylosing spondylitis
,
prolymphocytic leukemia t-cell
,
prolymphocytic leukemia
,
follicular lymphoma
,
non-hodgkin lymphoma
,
preleukemia
,
waldenstrom macroglobulinemia
,
macular degeneration
,
wet macular degeneration
,
ovarian neoplasms
,
fallopian tube neoplasms
,
ovarian epithelial carcinoma
,
hypersensitivity
,
rheumatoid arthritis
,
leukemia
,
lymphoid leukemia
,
crohn disease
,
b-cell chronic lymphocytic leukemia
,
lung neoplasms
,
non-small-cell lung carcinoma
,
ulcerative colitis
,
colitis
,
ulcer
,
small cell lung carcinoma
,
systemic lupus erythematosus
,
rheumatic diseases
,
infections
,
hidradenitis suppurativa
,
hidradenitis
,
arteritis
,
juvenile arthritis
,
vitiligo
,
alopecia areata
,
alopecia
,
communicable diseases
,
bacterial infections
,
methicillin-resistant staphylococcus aureus
,
staphylococcal skin infections
,
infectious skin diseases
,
bacterial skin diseases
,
cellulitis
,
disease progression
,
covid-19
,
virus diseases
,
respiratory syncytial viruses
,
hepatitis c
,
hepatitis b
,
hepatitis
,
hepatitis a
,
takayasu arteritis
,
aortic arch syndromes
,
giant cell arteritis
,
polymyalgia rheumatica
,
sleep wake disorders
,
dyssomnias
,
parasomnias
,
colorectal neoplasms
,
arthritis
,
atopic dermatitis
,
eczema
,
dermatitis
,
spondylarthritis
,
spondylitis
,
axial spondyloarthritis
,
psoriatic arthritis
,
psoriasis
,
neurodermatitis
,
prurigo
,
triple negative breast neoplasms
,
coronary artery disease
,
myocardial ischemia
,
inflammation
,
atherosclerosis
Globulin, immune
large b-cell lymphoma diffuse
,
b-cell lymphoma
,
oncogenes
,
mantle-cell lymphoma
,
small cell lung carcinoma
,
renal cell carcinoma
,
kidney neoplasms
,
glioblastoma
,
glioma
,
astrocytoma
,
follicular lymphoma
,
myelodysplastic syndromes
,
thrombocytopenia
,
aplastic anemia
,
preleukemia
,
pancytopenia
,
bone marrow failure disorders
,
cytopenia
,
electrocardiography
,
liver diseases
,
hepatic insufficiency
,
prostatic neoplasms
,
castration-resistant prostatic neoplasms
,
lymphoma
,
multiple myeloma
,
plasma cell neoplasms
,
non-small-cell lung carcinoma
,
non-hodgkin lymphoma
,
neoplasm metastasis
,
colonic neoplasms
,
rectal neoplasms
,
sarcoma
,
lung neoplasms
,
triple negative breast neoplasms
,
mucinous adenocarcinoma
,
inflammatory breast neoplasms
,
carcinoma
,
bcr-abl positive chronic myelogenous leukemia
,
myeloid leukemia chronic-phase
,
myeloid leukemia
,
myeloid leukemia accelerated phase
,
blast crisis
,
philadelphia chromosome
,
recurrence
,
cystadenocarcinoma
,
carcinoid tumor
,
ductal carcinoma breast
,
hemangiosarcoma
,
bone fractures
,
fracture healing
,
headache
,
post-traumatic headache
,
vitiligo
,
psoriasis
,
temporomandibular joint disorders
,
temporomandibular joint dysfunction syndrome
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
melanoma
,
kidney transplantation
,
graft rejection
,
kidney diseases
,
iga glomerulonephritis
,
edema
,
invasive hydatidiform mole
,
erythema
,
breast neoplasms
,
leukemia
,
precursor cell lymphoblastic leukemia-lymphoma
,
lymphoid leukemia
,
stomach neoplasms
,
asthma
,
thyroid diseases
,
adenocarcinoma
,
dyslipidemias
,
homozygous familial hypercholesterolemia
,
human influenza
,
atopic dermatitis
,
eczema
,
dermatitis
,
immunoglobulin g4-related disease
,
colorectal neoplasms
,
hyperlipidemias
,
neoplasms
,
hypercholesterolemia
,
vasculitis
,
graves ophthalmopathy
,
eye diseases
,
rheumatoid arthritis
,
arthritis
,
anti-neutrophil cytoplasmic antibody-associated vasculitis
,
bone neoplasms
,
giant cell tumor of bone
,
giant cell tumors
,
hyperlipoproteinemias
,
hyperlipoproteinemia type ii
,
neuromyelitis optica
,
t-cell lymphoma peripheral
,
t-cell lymphoma cutaneous
,
coronary artery disease
,
myocardial ischemia
,
atherosclerosis
Demand
chronic urticaria
,
urticaria
,
sickle cell anemia
,
arthritis
,
gouty arthritis
,
gout
,
macular degeneration
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